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Risdiplam

  • Synonyms: RG7916; RO7034067
  • ATC: M09AX10
  • Use: Lorem 
  • Chemical name: Lorem ipsum dolor sit amet, consetetur sadipscing elitr, sed diam
  • Formula: Lorem ipsum dolor sit amet,
  • MW:401.47 g/mol
  • CAS-RN:1825352-65-5
  • InChI Key:ASKZRYGFUPSJPN-UHFFFAOYSA-N
  • InChI:InChI=1S/C22H23N7O/c1-​14-​9-​18(26-​29-​11-​15(2)​24-​21(14)​29)​17-​10-​20(30)​28-​12-​16(3-​4-​19(28)​25-​17)​27-​8-​7-​23-​22(13-​27)​5-​6-​22/h3-​4,​9-​12,​23H,​5-​8,​13H2,​1-​2H3

Substance Classes

Synthesis Path










Substances Referenced in Synthesis Path

CAS-RN Formula Chemical Name CAS Index Name
22059-21-8 C4H7NO2 1-aminocyclo-propane carboxylic acid
42303-42-4 C6H11NO2 ethyl 1-aminocyclopropane carboxylate
79-04-9 C2H2Cl2O chloroacetyl chloride
C8H12ClNO3 ethyl 1-[(chloroacetyl)-amino]cyclopropane carboxylate
Lorem Lorem Lorem Lorem
Lorem Lorem Lorem Lorem
Lorem Lorem Lorem Lorem
Lorem Lorem Lorem Lorem
Lorem Lorem Lorem Lorem
Lorem Lorem Lorem Lorem
Lorem Lorem Lorem Lorem
Lorem Lorem Lorem Lorem
Lorem Lorem Lorem Lorem
Lorem Lorem Lorem Lorem
Lorem Lorem Lorem Lorem
Lorem Lorem Lorem Lorem

Trade Names

Country Trade Name Vendor Annotation
USA Lorem Lorem
EU Lorem Lorem
J Lorem Lorem
(wfm = withdrawn from market)

Formulations

  • Loremipsumdolorsitamet,consetetursadipscingelitr,

References

    • WO 9999 999999 (F. Hoffmann-La Roche; 28.03.2019; EP-prior. 22.09.2017).
    • EP 9 999 999 (F. Hoffmann-La Roche; 29.07.2020; EP-prior. 22.09.2017).
    • WO 9999 999999 (PTC Therapeutics, F. Hoffmann-La Roche; 15.08.2013; USA-prior. 10.02.2012).
    • US 9 999 999 (PTC Therapeutics, F. Hoffmann-La Roche; 15.08.2013; USA-prior. 10.02.2012).
    • WO 9999 999999 (PTC Therapeutics, F. Hoffmann-La Roche; 19.11.2015; USA-prior. 15.05.2014).
    • US 9 999 999 (PTC Therapeutics, F. Hoffmann-La Roche; 15.05.2019; USA-prior. 15.05.2014).
    • EP 9 999 999 (PTC Therapeutics, F. Hoffmann-La Roche; 09.10.2019; USA-prior. 15.05.2014).
  • Discovery of Risdiplam:

    • Ratni, H. et al., J. Med. Chem., (2018) 61(15), 6501-6517.
  • New treatment of spinal muscular atrophy:

    • WO 9999 999999 (F. Hoffmann-La Roche; 17.12.2020; EP-prior. 12.06.2019).
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