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Risdiplam
-
Synonyms:
RG7916; RO7034067
-
ATC:
M09AX10
-
Use:
Lorem
-
Chemical name:
Lorem ipsum dolor sit amet, consetetur sadipscing elitr, sed diam
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Formula:
Lorem ipsum dolor sit amet,
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MW:401.47 g/mol
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CAS-RN:1825352-65-5
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InChI Key:ASKZRYGFUPSJPN-UHFFFAOYSA-N
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InChI:InChI=1S/C22H23N7O/c1-14-9-18(26-29-11-15(2)24-21(14)29)17-10-20(30)28-12-16(3-4-19(28)25-17)27-8-7-23-22(13-27)5-6-22/h3-4,9-12,23H,5-8,13H2,1-2H3
Substances Referenced in Synthesis Path
CAS-RN |
Formula |
Chemical Name |
CAS Index Name |
22059-21-8 |
C4H7NO2 |
1-aminocyclo-propane carboxylic acid |
|
42303-42-4 |
C6H11NO2 |
ethyl 1-aminocyclopropane carboxylate |
|
79-04-9 |
C2H2Cl2O |
chloroacetyl chloride |
|
|
C8H12ClNO3 |
ethyl 1-[(chloroacetyl)-amino]cyclopropane carboxylate |
|
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Lorem |
Trade Names
Country |
Trade Name |
Vendor |
Annotation |
USA |
Lorem |
Lorem
|
|
EU |
Lorem |
Lorem
|
|
J |
Lorem |
Lorem
|
|
(wfm = withdrawn from market)
Formulations
- Loremipsumdolorsitamet,consetetursadipscingelitr,
References
-
- WO 9999 999999 (F. Hoffmann-La Roche; 28.03.2019; EP-prior. 22.09.2017).
- EP 9 999 999 (F. Hoffmann-La Roche; 29.07.2020; EP-prior. 22.09.2017).
- WO 9999 999999 (PTC Therapeutics, F. Hoffmann-La Roche; 15.08.2013; USA-prior. 10.02.2012).
- US 9 999 999 (PTC Therapeutics, F. Hoffmann-La Roche; 15.08.2013; USA-prior. 10.02.2012).
- WO 9999 999999 (PTC Therapeutics, F. Hoffmann-La Roche; 19.11.2015; USA-prior. 15.05.2014).
- US 9 999 999 (PTC Therapeutics, F. Hoffmann-La Roche; 15.05.2019; USA-prior. 15.05.2014).
- EP 9 999 999 (PTC Therapeutics, F. Hoffmann-La Roche; 09.10.2019; USA-prior. 15.05.2014).
-
Discovery of Risdiplam:
- Ratni, H. et al., J. Med. Chem., (2018) 61(15), 6501-6517.
-
New treatment of spinal muscular atrophy:
- WO 9999 999999 (F. Hoffmann-La Roche; 17.12.2020; EP-prior. 12.06.2019).